Q2 Update 2025

Glafabra's Progress Towards Repeating Fabry Trials in USA

Stem Cell Therapy for Fabry Disease

understand the therapeutic effect of cell therapy

Metabolic Enzyme Disorders

Explore the diversity of metabolic enzyme disorders

Options Agreement on Improved Lentivector

Announcement of signed agreement

Partnership with University of Utah Health

Announcement of signed agreement

Glafabra Welcomes Elizabeth Wagner to Advisory Board

View press release

New Fabry disease therapy shows 130x increase in effectiveness.

Details on effectiveness